Search All Tech Briefings


Search technology briefings produced by NIHR Innovation Observatory. These are short reports on new or repurposed medicines that we have already sent to our stakeholders. Only those technologies (medicines) that are within the scope of our stakeholders will have a technology briefing available.  Search our technology briefings by intervention (drug or device), specific indication (disease or condition), or general therapeutic area.

| 85 Results

Title
Intervention Indication Therapeutic Area Year Actions
Venglustat for treating late onset GM2 gangliosidosis, GM1 gangliosidosis and other ultra-rare disease Venglustat GM1 gangliosidosis , GM2 gangliosidosis Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2023 View  |  Download
Venglustat for treating type 3 Gaucher disease after 1 therapy Venglustat Gaucher disease Endocrine Nutritional and Metabolic Disorders , Genetic Disorders 2023 View  |  Download
Vestronidase alfa (UX-003) for mucopolysaccharidosis type VII (MPS 7; Sly syndrome) Vestronidase alfa (Mepsevii; rhGUS; UX003) Mucopolysaccharidosis type VII Endocrine Nutritional and Metabolic Disorders 2017 View  |  Download
Veverimer for metabolic acidosis associated with chronic kidney disease TRC101 (Veverimer) Metabolic acidosis Cardiovascular System , Endocrine Nutritional and Metabolic Disorders , Nephrology 2020 View  |  Download
Vutrisiran for treating hereditary transthyretin amyloidosis Vutrisiran (ALN-TTRSC02) Amyloidosis Endocrine Nutritional and Metabolic Disorders 2022 View  |  Download
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